Pasar al contenido principal

The ELEVIDYS impact

This section is a modal
Off
Lotties
1 - src: /sites/default/files/2026-07/Interior-Crescent-10-Green_0.json / styles: top: 315px; left: -797px; height: 1650px; position: absolute; / loop: On
2 - src: /sites/default/files/2026-07/Interior-Crescent-13-Green.json / styles: top: -680px; right: -253px; width: 521px;; height: 1307px; position: absolute; / loop: On

ELEVIDYS slowed disease progression*

based on multiple measures of everyday movement

North Star Ambulatory Assessment

ELEVIDYS helped people

score higher on tests of everyday movements

Time to rise

ELEVIDYS helped people

get up from the floor faster

10-minute walk run

ELEVIDYS helped people

walk/run faster

This section is a modal
Off
This section is a modal
Off

* Results were assessed at 1 year vs placebo and at 3 years vs external control. Additional assessments at 3 years are considered exploratory. Talk to your doctor to learn more.

This section is a modal
Off

With ELEVIDYS, participants scored higher on tests that measure everyday movements

as measured by the average change in NSAA (North Star Ambulatory Assessment) score

1 year after ELEVIDYS
1 year after ELEVIDYS
3 years after ELEVIDYS
3 years after ELEVIDYS
This section is a modal
Off
North Star Ambulatory Assessment

The NSAA looks at how well participants can perform 17 different everyday movements

Each movement is scored on a scale (0=the person cannot complete the movement at all; 1=they require help; 2=they can accomplish it independently). Scores are checked at different points to track changes over time. If a score increases by 1 or 2 points, it means a person maintained or improved their ability to perform that movement.

This section is a modal
Off

With ELEVIDYS, participants got up from the floor faster

as measured by the average change in time to rise from the floor

This section is a modal
Off
1 year after ELEVIDYS
graphic-test-time-to-rise-1-year-mobile
graphic-test-time-to-rise-3-year-desktop
graphic-test-time-to-rise-3-year-mobile
This section is a modal
Off
Time to rise

Getting up from the floor faster after treatment suggests a delay in disease progression

This section is a modal
Off

Additional assessments are considered exploratory. Talk to your doctor to learn more.

All participants had similar characteristics (eg, age, physical ability) at the start of the study and were on stable doses of steroids.

This section is a modal
Off

With ELEVIDYS, participants walked or ran faster

as measured by the average change in 10-meter walk/run time

1 year after ELEVIDYS
1 year after ELEVIDYS
3 years after ELEVIDYS
3 years after ELEVIDYS
This section is a modal
Off
10-minute walk run

Walking/running faster after treatment suggests a delay in disease progression

This section is a modal
Off

Next up: Explore micro-dystrophin results

Now that you’ve seen how ELEVIDYS can slow disease progression, learn more about how it directly addresses the absence of dystrophin in Duchenne.

Go

This section is a modal
Off
image-max-kite
This section is a modal
Off

Proven to produce ELEVIDYS micro-dystrophin

This section is a modal
Off
3 months after ELEVIDYS
16 months after ELEVIDYS
This section is a modal
Off
ELEVIDYS micro-dystrophin

The average increase in ELEVIDYS micro-dystrophin was consistent

People with Duchenne who are untreated typically have little to no dystrophin.

This section is a modal
Off
green divider
This section is a modal
Off

Next up: Explore muscle loss data

Now that you’ve seen how ELEVIDYS directly addresses the absence of dystrophin in Duchenne, learn more about its impact on muscle loss.

Go

This section is a modal
Off
Colton received ELEVIDYS in 2024
This section is a modal
Off